Biotech & Genomics
CRISPR-Cas9 Therapeutic Horizons: Direct In Vivo Genomic Editing in Clinical Hematology
Long-term follow-up from pioneering clinical trials confirms durable reconstitution of fetal hemoglobin in sickle cell disease and beta-thalassemia, heralding a new era of definitive genetic medicine.
Dr. Aris Thorne, MD
5 min2,890